The Kennedy’s Disease Association thanks all those that worked so hard to get this bill passed.
"We salute the Senate for decisive and bipartisan action in approving the FDA Safety and Innovation Act (S. 3187)," said Peter L. Saltonstall, president and CEO of NORD. "And we applaud the House of Representatives for approving in a similarly bipartisan manner the House version of this bill last week."
Saltonstall said the legislation, which now goes to President Obama for his signature, provides broad-ranging and innovative measures to speed the development of safe and effective treatments for people who desperately need them.
"Only about 250 of the nearly 7,000 diseases considered rare in the U.S. have therapies," he said. "But treatments are desperately needed because most rare diseases are serious, many are life-threatening, and about two-thirds of the patients are children."
He added that "NORD and its members have worked long and hard to raise awareness of the challenges of living with rare diseases. We are grateful for the hard work and thoughtful deliberation that both the House and Senate have brought to this process."
Among others, some features of the bill that Saltonstall said were especially important to NORD and the rare disease patient community include:
- enhancing accelerated patient access to new medical treatments
- encouraging the development of Humanitarian Use Devices, or medical devices for small patient populations
- providing for accelerated development of "breakthrough therapies" -- or ones that show early promise
- enhanced consultation with rare disease medical experts and
- a rare pediatric disease priority review voucher incentive program
The bill approved by the Senate today and the one approved by the House last week are the result of a process that has been underway for nearly two years and for which NORD has provided significant input, the reauthorization of the Prescription Drug User Fee Act (PDUFA). This legislation, which authorizes the Food and Drug Administration (FDA) to collect user fees from companies seeking to have products reviewed, must be reauthorized every five years.